Catalogue number: | PA 14 1380000 |
Chemical name: | Nusinersen Sodium |
CAS Number: |
NA |
Category: | peptides,peptides |
Synonyms: | NA |
Molecular form: | NA |
Appearance: | NA |
Mol. Weight: | NA |
Storage: | 2-8°C Refrigerator |
Shipping Conditions: | Ambient |
Applications: | An antisense oligonucleotide that induces survival motor neuron (SMN) protein expression, as Spinraza for the treatment of children and adults with spinal muscular atrophy (SMA). It is adminstrated as direct intrathecal injection. |
Nusinersen Sodium - API Standards
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